Capo, V; Penna, S; Merelli, I; Barcella, M; Scala, S; Basso-Ricci, L; Draghici, E; Palagano, E; Zonari, E; Desantis, G; Uva, P; Cusano, R; Sergi, L Sergi; Crisafulli, L; Moshous, D; Stepensky, P; Drabko, K; Kaya, Z; Unal, E; Gezdirici, A; Menna, G; Serafini, M; Aiuti, A; Locatelli, S L; Carlo-Stella, C; Schulz, A S; Ficara, F; Sobacchi, C; Gentner, B; Villa, A
Expanded circulating hematopoietic stem/progenitor cells as novel cell source for the treatment of ŦCIRG1 osteopetrosis Journal Article
In: Haematologica, 106 (1), pp. 74–86, 2021.
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title = {Expanded circulating hematopoietic stem/progenitor cells as novel cell source for the treatment of ŦCIRG1 osteopetrosis},
author = {V Capo and S Penna and I Merelli and M Barcella and S Scala and L Basso-Ricci and E Draghici and E Palagano and E Zonari and G Desantis and P Uva and R Cusano and L Sergi Sergi and L Crisafulli and D Moshous and P Stepensky and K Drabko and Z Kaya and E Unal and A Gezdirici and G Menna and M Serafini and A Aiuti and S L Locatelli and C Carlo-Stella and A S Schulz and F Ficara and C Sobacchi and B Gentner and A Villa},
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Capo, V; Castiello, M C; Fontana, E; Penna, S; Bosticardo, M; Draghici, E; Poliani, L P; Sergi, L Sergi; Rigoni, R; Cassani, B; Zanussi, M; Carrera, P; Uva, P; Dobbs, K; Sacchetti, N; Notarangelo, L D; van Til, N P; Wagemaker, G; Villa, A
Efficacy of lentivirus-mediated gene therapy in an Omenn syndrome recombination-activating gene 2 mouse model is not hindered by inflammation and immune dysregulation Journal Article
In: J Allergy Clin Immunol, 142 (3), pp. 928–941, 2018.
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title = {Efficacy of lentivirus-mediated gene therapy in an Omenn syndrome recombination-activating gene 2 mouse model is not hindered by inflammation and immune dysregulation},
author = {V Capo and M C Castiello and E Fontana and S Penna and M Bosticardo and E Draghici and L P Poliani and L Sergi Sergi and R Rigoni and B Cassani and M Zanussi and P Carrera and P Uva and K Dobbs and N Sacchetti and L D Notarangelo and N P van Til and G Wagemaker and A Villa},
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Schiroli, G; Ferrari, S; Conway, A; Jacob, A; Capo, V; Albano, L; Plati, T; Castiello, M C; Sanvito, F; Gennery, A R; Bovolenta, C; Palchaudhuri, R; Scadden, D T; Holmes, M C; Villa, A; Sitia, G; Lombardo, A; Genovese, P; Naldini, L
Preclinical modeling highlights the therapeutic potential of hematopoietic stem cell gene editing for correction of SCIĐ-X1 Journal Article
In: Sci Transl Med, 9 (411), 2017.
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title = {Preclinical modeling highlights the therapeutic potential of hematopoietic stem cell gene editing for correction of SCIĐ-X1},
author = {G Schiroli and S Ferrari and A Conway and A Jacob and V Capo and L Albano and T Plati and M C Castiello and F Sanvito and A R Gennery and C Bovolenta and R Palchaudhuri and D T Scadden and M C Holmes and A Villa and G Sitia and A Lombardo and P Genovese and L Naldini},
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Chiriaco, M; Farinelli, G; Capo, V; Zonari, E; Scaramuzza, S; Matteo, G Di; Sergi, L S; Migliavacca, M; Hernandez, R J; Bombelli, F; Giorda, E; Kajaste-Rudnitski, A; Trono, D; Grez, M; Rossi, P; Finocchi, A; Naldini, L; Gentner, B; Aiuti, A
Đual-regulated lentiviral vector for gene therapy of X-linked chronic granulomatosis Journal Article
In: Mol Ther, 22 (8), pp. 1472–1483, 2014.
@article{pmid24869932,
title = {Đual-regulated lentiviral vector for gene therapy of X-linked chronic granulomatosis},
author = {M Chiriaco and G Farinelli and V Capo and E Zonari and S Scaramuzza and G Di Matteo and L S Sergi and M Migliavacca and R J Hernandez and F Bombelli and E Giorda and A Kajaste-Rudnitski and D Trono and M Grez and P Rossi and A Finocchi and L Naldini and B Gentner and A Aiuti},
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